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DEVELOPMENT pipeline

Updated in January 2026

Oncology

SOLID TUMORS

Compound / MOA
Project
Therapeutic area
Phase
Darovasertib
S247629
Uveal melanoma
DPC
1
2
3
Ivosidenib
S95031
Chondrosarcoma
DPC
1
2
3
Ivosidenib + Durvalumab + Gemcitabine/Cisplatine
S95031
Cholangiocarcinoma
DPC
1/2
3
Vorasidenib + temozolomide
S95032
Glioma
DPC
1
2
3
Vorasidenib + pembrolizumab
S95032
Glioma
DPC
1
2
3
Anti-TIM3 combo
S95018
Non-small Cell Lung Cancer + in association
DPC
1/2
3
Anti-CD73 combo
S95024
Non-small Cell Lung Cancer + in association
DPC
1/2
3
Anti-NKG2A combo
S95029
Non-small Cell Lung Cancer + in association
DPC
1/2
3
Anti-NKG2A combo
S95029
Gastric cancer
DPC
1/2
3
MAT2A inhibitor
S95035
Solid tumors
DPC
1/2
3
RAS/RAF inhibitor
S241656
Solid tumors
DPC
1/2
3
ND
S234821
Solid tumors
DPC
1
2
3

HEMATOLOGICAL MALIGNANCIES

Compound / MOA
Project
Therapeutic area
Phase
Ivosidenib + 7+3 (chimio)
S95031
Acute Myeloid Leukemia (new indication)
DPC
1
2
3
Ivosidenib /
Azacitidine / Venetoclax
S95031
Acute Myeloid Leukemia (new indication)
DPC
1
2
3
Ivosidenib
S95031
Acute Myeloid Leukemia (new indication)
DPC
1
2
3
Menin inhibitor
S243249
Acute Myeloid Leukemia
Acute Lymphoblastic Leukemia
DPC
1
2
3
ND
S236220
Hematological malignancies
DPC
1
2
3
ND
S247567
Hematological malignancies
DPC
1
2
3

Neurology

Compound / MOA
Project
Therapeutic area
Phase
BK channel modulator
S247240
Fragile X syndrome
DPC
1/2
3
KCNT1 ASO
S230815
Developmental and epileptic encephalopathies AntiSensOligonucleotid
DPC
1/2
3
ND
S233107
Developmental and epileptic encephalopathies AntiSensOligonucleotid
DPC
1
2
3

PCD= Preclinical development phase, 1 = Phase 1, 2 = Phase 2, 3 = Phase 3, ND= Not disclosed